Clinical Study

A Phase 3 Randomized, Multicenter, Multinational, Double-Blinded Study Comparing The Efficacy And Safety Of Repeated Biweekly Infusions Of Neogaa (Gz4

Posted Date: May 15, 2019

  • Investigator: Hani Kushlaf
  • Specialties:
  • Type of Study: Drug

The purpose of this study is to evaluate the possible risks and efficacy (improvement of disease), as well as pharmacokinetics (breakdown, use and removal from the body of the study drug (neoGAA) of the study drug (neoGAA) compared to Myozyme?/Lumizyme? (alglucosidase alfa) in the treatment of patie


To Be Considered For This Study, You Must Have Been Diagnosed With Late Onset Pompe Disease (Acid A


Abnormal Emg, Myopathy, Pompe, Elevated Liver Enzym, Enzyme Replacement T

For More Information:

Molly Winters

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